Breakthrough · April 1, 2026
FDA Approves First Therapy to Treat Neurological Decline in Rare Hunter Syndrome
A newly FDA-approved drug gives hope to families racing to save their children's lives from serious illness....
Treatment · March 25, 2026
FDA Approves First Brain-Penetrating Therapy for Hunter Syndrome in Decades
FDA approves the first new Hunter Syndrome treatment in nearly two decades, offering hope to patients with this rare genetic disea...
Pediatrics · March 21, 2026
New Drug Awaits FDA Decision Offering Hope for Children With Fatal Hunter Syndrome
A mother's urgent advocacy for FDA approval of a new drug offers hope for children suffering from terminal Hunter Syndrome....
Breakthrough · November 26, 2025
Early Gene Therapy Trial Shows Promise for Treating Hunter Syndrome
Gene therapy shows early promise in treating Hunter Syndrome, offering hope to affected families....