Treatment · May 26, 2026
Boy With Muscle-Wasting Disease Wins Access to Lifesaving New Drug
A father celebrates his son's ability to access a new life-changing drug, bringing hope to families....
Treatment · May 14, 2026
Duchenne Gene Therapy Hits Key Protein Target as FDA Filing Nears
Regenxbio's positive new data brings hope closer to patients with Duchenne muscular dystrophy seeking gene therapy treatment....